SMA6 小时
The nature of devastation, from SMA to Helene, and a resilient spirit
Columnist Helen Baldwin describes the destruction from Hurricane Helene and comments on the resilient spirit of people facing ...
SMA7 小时
Newborns given Evrysdi reaching key milestones after 2 years
The babies were treated before symptom onset, and are sitting, standing, and walking independently, many consistent with ...
SMA1 天
What it means to go the distance while living with SMA
As his 31st birthday approaches, columnist Kevin Schaefer reflects on how he goes at his own pace while living with SMA.
SMA2 天
CASMA, large-scale screening test, may best detect SMA carriers
Scientists compared the CASMA screening approach against standard methods, and found it better at detecting problems in genes ...
SMA6 天
When the disabled needed a place to connect, I created one
Sensing her need to connect with others in the disability community, columnist Jasmine Ramos created The Friendship Circle.
SMA5 天
High dose of SMA treatment Spinraza shows benefits: Trial data
A high-dose regimen of SMA treatment Spinraza benefits for previously treated and untreated SMA patients of all ages, per ...
SMA7 天
Apitegromab hits goal of boosting motor function in Phase 3 trial
Scholar Rock’s apitegromab led to motor function improvements over a year of treatment in young adults and children with spinal muscular atrophy (SMA) type 2 or 3 who could sit independently and were ...