How can you measure a person's quality of life? For columnist Patrick Moeschen, the key is deciding for yourself what a good ...
Columnist Shalom Lim appreciates how Duchenne never offers a dull moment as he prepares for the challenges and adventures in ...
FSHD exacts a toll on columnist Robin Stemple when he is out and about. He calls these symptom flares "FSHD hangovers." ...
Sevasemten significantly reduced two markers of muscle damage in treated Becker muscular dystrophy patients in Phase 2 CANYON ...
Agamree (vamorolone) was recommended for use in the NHS in England, Wales, and Northern Ireland for treating Duchenne ...
Learning that three of her sons had DMD challenged columnist Betty Vertin, but now she embraces the highs and lows of the experience.
The Muscular Dystrophy Association (MDA) has awarded nearly two dozen new grants to fund research into various forms of muscular dystrophy, including Duchenne and limb-girdle, as well as related ...
Arrakis Therapeutics’ investigational RNA-targeted small molecule (rSM) therapies were found to work as intended in preclinical studies and eased symptoms in a mouse model of myotonic dystrophy type 1 ...