CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

So we have to change society. It’s a tall order, but it’s been done over and over again throughout history. It starts with a ...

Hurricanes in the southeastern U.S. prompt columnist Robin Stemple, who has FSHD, to consider his emergency preparedness plan ...

Treatment with an RNA-based therapy approach was found to correct molecular defects in a cell model of myotonic dystrophy ...

Columnist Betty Vertin, watching her son Chance complete his final season, wishes her sons with DMD could've played football, too.